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polyglutamine expansion disorder

Genetic disorders associated with CAG trinucleotide repeat expansions.

Specific

dentatorubral-pallidoluysian atrophy (DRPLA) Huntington disease-like type 2 Huntington's disease; Huntington's chorea (progressive hereditary chorea) olivopontocerebellar atrophy type 1 (Menzel type); spinocerebellar ataxia type 1 (SCA-1) spinocerebellar ataxia type 17 (SCA-17) spinocerebellar ataxia type 2 (SCA-2); olivopontocerebellar atrophy, Holguin type spinocerebellar ataxia type 3 (SCA-3); Machado-Joseph disease; Azorean disease spinocerebellar ataxia type 6 (SCA-6) spinocerebellar ataxia type 7 (SCA-7); olivopontocerebellar atrophy type 3 (retinal degeneration) X-linked bulbospinal muscular atrophy (Kennedy's disease)

General

neurodegenerative disease trinucleotide repeat expansion disease

References

  1. Li & Li. Trends Genet. 2004 Mar;20(3):146-54 PMID: 15036808