Contents

Search


ivacaftor

Indications: - cystic fibrosis patients with at least 1 CFTR mutation G551D - used in combination with lumacaftor for treatment of cystic fibrosis CFTR F508del mutation [2] Dosage: - 150 mg PO every 12 hours Mechanism of action: - CFTR potentiator

General

pulmonary agent heterocyclic compound, 1 ring amide phenol

Database Correlations

PUBCHEM cid=16220172

References

  1. Ramsey BW et al. A CFTR potentiator in patients with cystic fibrosis and the G551D mutation. N Engl J Med 2011 Nov 3; 365:1663. PMID: 22047557 - Davis PB. Therapy for cystic fibrosis - The end of the beginning? N Engl J Med 2011 Nov 3; 365:1734. PMID: 22047565
  2. FDA News Release. July 2, 2015 FDA approves new treatment for cystic fibrosis http://www.fda.gov/NewsEvents/Newsroom/PressAnnouncements/ucm453565.htm

Component-of

elexacaftor/ivacaftor/tezacaftor ivacaftor/lumacaftor (Orkambi) ivacaftor/tezacaftor