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Dyggve-Melchior-Clausen syndrome

Epidemiology: rare Pathology: - electron microscopy - cutaneous cells of affected patients show - dilated rough endoplasmic reticulum - enlarged & aberrant vacuoles - numerous vesicles Genetics: 1) autosomal recessive 2) associated with defect in dymeclin gene Clinical manifestations: 1) short trunk dwarfism 2) microcephaly 3) psychomotor retardation 4) progressive disorder

General

genetic syndrome (multisystem disorder) developmental disorder

Database Correlations

OMIM 223800

References

OMIM :accession 223800