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alpha-methylacyl-CoA racemase (AMACR) deficiency

Genetics: - associated with defects in AMACR Clinical manifestations: - adult onset sensory motor neuropathy Laboratory: - elevated concentrations of pristanic acid (serum,urine ?) - alpha-methylacyl CoA racemase in fibroblasts

General

lipid metabolism, inborn error; lipid storage disease; lipidosis

Database Correlations

OMIM 604489

References

OMIM :accession 604489