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POEMS syndrome (Polyneuropathy, Organomegaly, Endocrinopathy, Monoclonal gammopathy, & Skin changes); Crow-Fukase syndrome

Etiology: - monoclonal gammopathy of uncertain significance - multiple myeloma - solitary plasmacytoma of bone Epidemiology: - rare Pathology: - vasculopathy (non-inflammatory) [1] - demyelination [2] Clinical manifestations: - demyelinating sensorimotor polyneuropathy - ascending muscle weakness [2] (one case) - diminished reflexes [2] (one case) - organomegaly (hepatosplenomegaly) - endocrinopathy - hypogonadism - adrenal insufficiency - hypothyroidism - diabetes mellitus - monoclonal gammopathy - skin & skin appendage changes - hyperpigmentation - hypertrichosis - pitting edema [2] (one case) - multicentric Castleman's disease - osteosclerosis - development over a 5 month period [2] (one case) Diagnostic criteria: - diagnosis of which requires evidence of a demyeliniating polyneuropathy & a lambda monoclonal gammopathy, plus at least one other major criterion & one minor criterion - major criteria - sclerotic bone lesion - elevated plasma VEGF level - Castleman's disease (angiofollicular lymph node hyperplasia) [4] - minor criteria - organomegaly - fluid overload - papilledema - endocrinopathy: hypothyroidism, diabetes mellitus - skin changes - thrombocytosis & polycythemia - papilledema [4] Laboratory: - thyroid function tests - serum protein electrophoresis (paraproteinemia) - plasma VEGF markedly elevated [2] - serum testosterone may be low [3] - bone marrow biopsy [2] - interstitial plasmacytosis consistent with plasma-cell dyscrasia - lumbar puncture: CSF analysis - fat pad biopsy: no evidence of amyloidosis [2] Special laboratory: - nerve conduction studies [2] (one case) - reduced sensory & motor-nerve conduction velocities - prolonged F responses - electromyography [2] (one case) - recruitment with abnormal spontaneous activity in the distal muscles of the lower extremities - ophthalmoscopy - optic disks were diffusely swollen [2] (one case) Radiology: - MRI of the spine - no evidence of mass lesion [2] (one case) - MRI of the brain: normal [2] (one case) - abdominal ultrasound: hepatosplenomegaly - echocardiogram [2] (one case) - pulmonary hypertension - right ventricular hypertrophy - tricuspid regurgitation - pericardial effusion Complications: - independent risk factor for stroke - cerebral arterial thromboses [1] - lower limb peripheral arterial thrombosis Management: - patients with 1-3 bone lesions & no clonal plasma cells on bone marrow biopsy, radiation therapy 45 Gy is preferred [4] - oral glucocorticoid therapy with high-dose dexamethasone - bortezomib in combination with dexamethasone & cyclophosphamide [4] - lenalidomide in combination dexamethasone [4] - daratumumab or ixazomib in combination with lenalidomide & dexamethasone [4] - referral for stem cell transplantation - high-dose melphalan conditioning - autologous stem-cell transplantation [2] (one case) Notes: - Review article June 2021 [4]

Interactions

disease interactions

General

paraproteinemia (monoclonal gammopathy) peripheral nerve disease; peripheral neuropathy

References

  1. Dupont SA et al Cerebral infarction in POEMS syndrome: Incidence, risk factors, and imaging characteristics. Neurology 2009 Oct 20; 73:1308. PMID: 19841383
  2. Smith C et al Clinical problem-solving. Diagnosing One Letter at a Time. N Engl J Med 2015; 372:67-73. January 1, 2015 PMID: 25551528 http://www.nejm.org/doi/full/10.1056/NEJMcps1308732
  3. Medical Knowledge Self Assessment Program (MKSAP) 17, 18. American College of Physicians, Philadelphia 2015, 2018
  4. Khouri J, Nakashima M, Wong S Update on the Diagnosis and Treatment of POEMS (Polyneuropathy, Organomegaly, Endocrinopathy, Monoclonal Gammopathy, and Skin Changes) Syndrome. A Review. JAMA Oncol. Published online June 3, 2021 PMID: 34081097 https://jamanetwork.com/journals/jamaoncology/fullarticle/2780474