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Specific
acetic acid
acetohydroxamic acid (Lithostat)
acetylcarnitine
adenosine monophosphate (AMP)
agalsidase beta (Fabrazyme, Replagal)
Aldurazyme (alpha-L-iduronidase)
alglucerase (Ceredase)
alglucosidase alfa (Myozyme, Lumizyme)
allopurinol (Zyloprim, Lopurin, Zurinol)
alpha-1-antitrypsin; alpha-1 protease inhibitor; alpha-1-antiproteinase; Serpin A1 (SERPINA1, AAT, PI, PRO0684, PRO2209)
alpha-L-iduronidase (laronidase, Aldurazyme, IDUA)
ammonia aromatic spirits
ammonium chloride
antimetabolite
aramchol
Asentar
asfotase alfa (Strensiq)
avalglucosidase alfa-ngpt (Nexviazyme)
bempedoic acid (Nexletol)
benphothiamine; benfothiamine; S-Benzoylthiamine O-monophosphate (Biotamin, Berdi)
berotralstat (Orladeyo)
bicarbonate/carbonate (Carbicarb)
Bio factor
Brain Pep
bremelanotide (Vyleesi)
burosumab
butafosfan
calcimimetic
calcium & magnesium citrate
calcium chloride
calcium glubionate (Calcionate, Neo-Calglucon)
calcium gluceptate
calcium gluconate
calcium glycerophosphate (Prelief)
calcium hydrogen phosphate (Ca[HPO4])
calcium iodide
calcium lactate (Calphosan)
calcium magnesium phosphate
calcium phosphate (Ca3[PO4]2)
calcium supplement
carboxymethylcellulose/sorbitol (artificial saliva, saliva substitute)
carglumic acid (Carbaglu)
carnitine (Carnitor)
casimersen (Amondys 45)
chelated chromium
chelated potassium
chromic chloride; chromium(III) chloride; chromium trichloride; CrCl3
chromium picolinate
chromous chloride; chromium(II) chloride; chromium dichloride; CrCl2
citrate (citric acid)
CO2 (carbon dioxide, carbonic anhydride)
colchicine (Colcrys, Lodoco)
copper gluconate
crystalloid
cupric chloride; copper bichloride; copper(II) chloride; Coppertrace (CuCl2)
Cyanokit
cysteamine; 2-aminoethanethiol (Cystagon)
dihydroxyacetone (glycerone)
dirlotapide (Slentrol)
elamipretide
elapegademase (Revcovi)
eliglustat (Cerdelga)
elosulfase alfa (Vimizim)
enzyme replacement
eplontersen (Wainua)
eteplirsen (Exondys)
ezutromid
febuxostat (Uloric)
focus factor
Folgard Rx 2.2 (folate, B12, B6)
fosdenopterin; cyclic pyranopterin monophosphate; cPMP (Nulibry)
Freamine (8.5% & 10% amino acids)
fructose
gallium nitrate (Ganite)
givinostat (Duvyzat)
givosiran (Givlaari)
gluconolactone
glucosamine (Cosamin, Osteo-Bi-Flex)
glucose (dextrose, D-glucose)
glycerol/phospholipid/soy oil; Liposyn (10% & 20% fat emulsion)
golodirsen; Vyondys 53
guanidine
H2O (water molecule)
hydrochloric acid (HCl)
Hylenex (Wydase, Amphadase, Vitrase, Hydase, hyaluronidase)
Idursulfase (iduronate-2-sulfatase)
inotersen (Tegsedi)
lactase phlorizin hydrolase; lactase glycosylceramidase; lactase (LCT, LPH)
lactose
lipotropic
lumasiran (Oxlumo)
magnesium lactate
manganese chloride
manganese gluconate
manganese sulfate
mannose
metafolin (levomefolate calcium)
metreleptin (Myalepta)
migalastat (Galafold)
miglustat (Acetlion, Zavesca, Opfolda)
Mindpro
molybdenum salt
muvalaplin
nitisinone (Orfadin)
O2 (molecular oxygen)
olipudase alfa-rpcp (Xenpozyme)
omega-3-fatty acid ethyl esters (Omacor, Lovaza)
omega-3-fatty ester
orlistat (Xenical, Alli)
palm oil (red palm oil)
palovarotene (Sohonos)
patiromer (Veltassa)
pegademase bovine (Adagen)
pegunigalsidase alfa-iwxj (Elfabrio)
pegvaliase (Palynziq)
pharmaceutical magnesium
phenylbutyrate (Buphenyl, Olpruva)
phosphate binder
phosphatidylserine
polystyrene sulfonate (Kayexalate, Kalimate, Kionex)
potassium bicarbonate (Effer-K, K-lyte)
potassium bromide (KBr)
potassium iodide (KI, Thyro-Block, Irostat)
potassium salt unspecified
Promega (omega-3-fatty acids)
PTC124
ranolazine (Ranexa)
romosozumab (Evenity)
S-adenosyl methionine (AdoMet, SAM, ademetionine)
sacrosidase (Sucraid)
sapropterin (Kuvan)
sebelipase alfa (Kanuma)
selenious acid; selenite (Sele-Pak, Selepen)
sodium acetate (NaOAc)
sodium bicarbonate (NaHCO3)
sodium chloride (NaCl, Adsorbonac Ophthalmic)
sodium citrate/citric acid (Bicitra)
sodium gluconate
sodium iodide (Iodopen, NaI)
sodium lactate
sodium phosphate (NaH2PO4)
sodium zirconium cyclosilicate (Lokelma, ZS-9)
soluble guanylate cyclase stimulator
somapacitan-beco (Sogroya)
soy oil
stannous fluoride (SnF2, Fluoristan)
strontium ranelate (Protelos)
strontium [Sr]
sucrose
tafamidis; tafamidis meglumine (Vyndaqel. Vyndamax)
taliglucerase alfa (Elelyso)
taurine; 2-aminoethylsulfonic acid
tenapanor (Ibsrela)
tiopronin; alpha-mercaptopropionylglycine (Tiola)
trace metals for injection
tromethamine; 2-amino-2-(hydroxymethyl)propane-1,3-diol
uridine triacetate (Xuriden)
urinary acidifier
urinary alkalinizer
velaglucerase alfa (Vpriv)
velmanase-alfa (Lamzeda)
vestronidase alfa-vjbk (Mepsevii)
viltolarsen (Viltepso)
vitamin
vosoritide (Voxzogo)
VX-770
zinc supplement
General
pharmaceutical agent