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Hermansky-Pudlak syndrome 1/HPS1 mutation

Pathology: - see Hermansky-Pudlak syndrome Genetics: - associated with frameshift mutations in HPS1

Database Correlations

OMIM 203300

References

- Oh J et al. Positional cloning of a gene for Hermansky-Pudlak syndrome, a disorder of cytoplasmic organelles. Nat Genet. 1996 Nov;14(3):300-6. PMID: 8896559