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glycogen storage disease type-IXc (autosomal liver glycogenosis)

Genetics: - caused by defects in PHKG2 gene Clinical manifestations: 1) manifestations in infancy 2) hepatomegaly 3) growth retardation Laboratory: 1) elevated serum ALT, serum AST 2) lipid panel: dyslipidemia

Properties

DEFICIENT-PROTEIN: phosphorylase kinase COMPARTMENT: cytoplasm STATE: active state MOTIF: S/T-phosphate kinase domain MOTIF: ATP-binding site NAME: ATP-binding site calmodulin binding site EFFECTOR-BOUND: calmodulin

Database Correlations

OMIM 172471

References

OMIM :accession 605598